Ivacaftor treatment of cystic fibrosis in children aged 12 to <24 months and with a CFTR gating mutation (ARRIVAL): a phase 3 single-arm study
Rosenfeld, Margaret⋅Wainwright, Claire E⋅Higgins, Mark⋅Wang, Linda T⋅McKee, Charlotte⋅Campbell, Daniel⋅Tian, Simon⋅Schneider, Jennifer⋅Cunningham, Steve⋅Davies, Jane C⋅Rosenfeld, Margaret⋅Wainwright, Claire E⋅Higgins, Mark⋅Wang, Linda T⋅McKee, Charlotte⋅Campbell, Daniel⋅Tian, Simon⋅Schneider, Jennifer⋅Cunningham, Steve⋅Davies, Jane C⋅Harris, William⋅Mogayzel, Peter⋅McCoy, Karen⋅Milla, Carlos⋅Rubenstein, Ronald⋅Walker, Seth⋅Black, Philip⋅Montgomery, Gregory⋅McColley, Susanna⋅Hiatt, Peter⋅Sawicki, Gregory⋅Rock, Michael⋅Aurora, Paul⋅Ratjen, Felix⋅Maitra, Anirban⋅Ives, Andrew⋅Gaillard, Erol⋅McNalley, Paul⋅Selvadurai, Hiranjan and Robinson, Philip
The Lancet Respiratory Medicine, vol. 6, (no. 7), pp. 553, July 2018. | Journal Article